亨廷顿病的希望：新疗法减缓疾病进展

Huntington’s Hopes After years of heartbreak, a new treatment slows this devastating disease EVERY WEEK neurologist Victor Sung sees people with Huntington’s disease, a rare and deadly neurodegenerative disorder, at his clinic at the University of Alabama at Birmingham. But a Wednesday last September was a day unlike any other. “I cried with every single patient,” Sung says. The results of crucial phase 1/2 clinical trials had finally been released: an experimental gene therapy drug was the first treat- ment that appeared to slow the progres- sion of Huntington’s. When someone is diagnosed with Huntington’s, their treatment options are limited. …